After Little Mix star Jesy Nelson's revelation that her twins have SMA, parents speak about their children's late diagnoses.
Late-stage trial data for Roche’s drug against muscle-wasting Elevidys showed positive results after two years of treatment for male patients aged 4 or older with Duchenne muscular dystrophy. The data ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
Oct 31 (Reuters) - Sarepta Therapeutics shares (SRPT.O), opens new tab fell nearly 44% on Tuesday, after its gene therapy for a progressive muscle-wasting disorder failed to meet the main goal in a ...
Jan 25 (Reuters) - PTC Therapeutics (PTCT.O), opens new tab said on Thursday the European health regulator's advisory panel reaffirmed a negative opinion for its drug used to treat an inherited ...
University of Pittsburgh School of Medicine researchers carrying out a small pilot clinical trial demonstrating that a drug-free, minimally invasive intervention targets the root cause of progressive ...
On Sunday, Jesy Nelson, a former member of beloved girl group Little Mix, shared the emotional news that her eight-month-old ...
Cancer cachexia is a multifactorial syndrome marked by a severe loss of body weight due primarily to the wasting of skeletal muscle and adipose tissue. This syndrome is often accompanied by systemic ...
Little Mix singer Jesy Nelson took to Instagram and shared the heartbreaking news her twins, Ocean Jade and Story Monroe, had ...