Singer Jesy Nelson has opened up sharing that her twin daughters have been diagnosed with Spinal Muscular Atrophy, but what ...

Spinal muscular atrophy with respiratory distress (SMARD) is a rare genetic condition that typically affects infants and children. It causes muscle weakness and breathing problems. Spinal muscular ...

British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.

—A new qualitative participatory study explored how powered mobility (PM), in the form of modified ride-on cars, impacts children with spinal muscular atrophy type 1 (SMA1) and their families. Here ...

Little Mix alum Jesy Nelson opened up in an emotional video Jan. 4 about her twin daughters’ Spinal Muscular Atrophy Type 1 diagnosis, a life-threatening disease that leads to severe muscle weakness.

Injections for spinal muscular atrophy (SMA) refer to two treatments that the Food and Drug Administration (FDA) has approved for SMA: nusinersen (Spinraza) and onasemnogene abeparovec-xioi (Zolgensma ...

Researchers evaluated oxygen saturation and arterial CO2 variables to screen for sleep disordered breathing in children with SMA type 1-3. Of the measures evaluated, only an oxygen desaturation index ...

The least-squares mean difference in the Hammersmith Functional Motor Scale-Expanded change from baseline at 12 months was 1.8 points for those 2 to 12 years receiving apitegromab vs placebo.

Spinal muscular atrophy explained after Jesy Nelson reveals her twins’ diagnosis - The singer shared an emotional update ...

PHILADELPHIA--(BUSINESS WIRE)--Exegenesis Bio, a rapidly growing global genetic medicines company, is pleased to announce the presentation of clinical efficacy and safety data from its EXG001-307 ...

After Jesy Nelson shared that her twin daughters were diagnosed with Spinal Muscular Atrophy Type 1, the Little Mix alum ...